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beta thalassaemia major

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Thalassemia Major Trial in Ferrara (Blood component A, Blood component B)

Completed
  • Thalassemia Major
  • Blood component A
  • Blood component B
  • Ferrara, Italy
    Day Hospital Thalassaemia and Haemoglobinopathies (DHTE)
Nov 11, 2021

Transfusion Dependent Beta-Thalassaemia Trial in Nanning (ET-01)

Recruiting
  • Transfusion Dependent Beta-Thalassaemia
  • ET-01
  • Nanning, Guangxi, China
    PLA 923 Hospital
Mar 2, 2023

Bone Denisty Change in Children With Beta Thalassemia Major

Not yet recruiting
  • Evaluate Bone Denisty Changes in Children With Beta Thalassemia Major
  • Dexa scan
  • (no location specified)
Sep 29, 2023

Transfusion Dependent Beta-Thalassaemia Trial in Guangzhou, Shenzhen, Tianjin (ET-01)

Active, not recruiting
  • Transfusion Dependent Beta-Thalassaemia
  • ET-01
  • Guangzhou, Guangdong, China
  • +3 more
May 9, 2022

Beta Thalassaemia Trial in Milan (Safety and Efficacy assessments)

Active, not recruiting
  • Beta Thalassaemia
  • Safety and Efficacy assessments
  • Milan, Italy
    Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR
Nov 22, 2022

Transfusion Dependent Beta-Thalassaemia Trial in Tianjin (ET-01)

Active, not recruiting
  • Transfusion Dependent Beta-Thalassaemia
  • ET-01
  • Tianjin, Tianjin, China
    Institute of Hematology & Blood Diseases Hospital
Dec 9, 2021

ß-thalassemia Trial in Shenzhen (ß-globin restored autologous hematopoietic stem cells)

Recruiting
  • β-thalassemia
  • β-globin restored autologous hematopoietic stem cells
  • Shenzhen, Guangdong, China
    Shenzhen Children's Hospital
Feb 24, 2023

MDD, Anhedonia Trial in Tallahassee (Delta-beta tACS via the Neurocare Direct Current Stimulator Multi-Channel 4, Theta-gamma

Not yet recruiting
  • Major Depressive Disorder
  • Anhedonia
  • Delta-beta tACS via the Neurocare Direct Current Stimulator Multi-Channel 4
  • +2 more
  • Tallahassee, Florida
    Florida State University
Nov 9, 2023

MDD Trial in Chapel Hill (Delta-beta cross-frequency transcranial alternating current stimulation via the NeuroConn

Recruiting
  • Major Depressive Disorder
  • Delta-beta cross-frequency transcranial alternating current stimulation via the NeuroConn DC-STIMULATOR MC
  • +2 more
  • Chapel Hill, North Carolina
    University of North Carolina at Chapel Hill
Jan 31, 2023

Non-transfusion-dependent Thalassemia, Low Risk Myelodysplastic Syndrome, Very-Low Risk Myelodysplastic Syndrome Trial in

Recruiting
  • Non-transfusion-dependent Thalassemia
  • +2 more
  • Düsseldorf, Germany
  • +19 more
Mar 18, 2022

Beta-Thalassemia Trial (CS-101 injection)

Not yet recruiting
  • Beta-Thalassemia
  • CS-101 injection
  • (no location specified)
Sep 27, 2023

Beta-Thalassemia Trial in Ferrara, Firenze, Pisa (Sirolimus 0.5 mg)

Recruiting
  • Beta-Thalassemia
  • Sirolimus 0.5 mg
  • Ferrara, FE, Italy
  • +3 more
Nov 11, 2021

Beta-Thalassemia Trial in Bulgaria, Israel, United States (VIT-2763 60 mg QD, VIT-2763 60 mg BID, VIT-2763 120 mg BID)

Withdrawn
  • Beta-Thalassemia
  • VIT-2763 60 mg QD
  • +3 more
  • Whittier, California
  • +6 more
Nov 7, 2022

Thalassemia Major, Transfusion-dependent Anemia Trial in Guangzhou (Luspatercept Injectable Product)

Recruiting
  • Thalassemia Major
  • Transfusion-dependent Anemia
  • Luspatercept Injectable Product
  • Guangzhou, Guangdong, China
    The second affiliated hospital of Sun Yat-sen University
Jul 15, 2022

Beta Thalassemia Major, Beta Thalassemia Intermedia Trial in Worldwide (SOTATERCEPT (ACE-011))

Completed
  • Beta Thalassemia Major
  • Beta Thalassemia Intermedia
  • SOTATERCEPT (ACE-011)
  • Créteil, France
  • +14 more
Aug 18, 2022

Thalassemia Major Trial (n-acetylcystine)

Not yet recruiting
  • Thalassemia Major
  • (no location specified)
Mar 9, 2023

MDD, Anhedonia Trial in Chapel Hill (Cross-frequency transcranial alternating current stimulation via the NeuroConn Direct

Recruiting
  • Major Depressive Disorder
  • Anhedonia
  • Cross-frequency transcranial alternating current stimulation via the NeuroConn Direct Current Stimulator Plus
  • Chapel Hill, North Carolina
    University of North Carolina at Chapel Hill
Oct 21, 2022

Transfusion Dependent Beta Thalassemia, Hemoglobinopathies, Thalassemia Major Trial in Nashville (EDIT-301)

Recruiting
  • Transfusion Dependent Beta Thalassemia
  • +3 more
  • EDIT-301
  • Oakland, California
  • +3 more
Jan 3, 2023

Beta Thalassemia Major Trial in Tirana (Emeramide)

Completed
  • Beta Thalassemia Major
  • Tirana, Albania
    University Hospital Center "Mother Theresa" Tirana
Aug 20, 2021

Beta Thalassemia Major Anemia Trial (blood sampling)

Not yet recruiting
  • Beta Thalassemia Major Anemia
  • blood sampling
  • (no location specified)
Jul 5, 2021

Thalassemia, Beta, Thalassemia Major Trial in Tianjin (VGB-Ex01)

Not yet recruiting
  • Thalassemia, Beta
  • Thalassemia Major
  • VGB-Ex01
  • Tianjin, Tianjin, China
    Regenerative Medicine Center
Sep 11, 2023

MDD, Major Depressive Episode Trial in Le Kremlin Bicetre (Venlafaxine extended release)

Completed
  • Major Depressive Disorder
  • Major Depressive Episode
  • Venlafaxine extended release
  • Le Kremlin Bicetre, France
    CHU de Bicetre
Aug 25, 2021

"Iron Overload and Endocrinological Diseases"

Recruiting
  • Iron Overload
  • +4 more
    • Modena, Italy
      Unit of Endocrinology of Azienza Ospedaliero-Universitaria di Mo
    Nov 13, 2023

    Beta Thalassemia Major Anemia Trial (SP-420)

    Not yet recruiting
    • Beta Thalassemia Major Anemia
    • (no location specified)
    Jan 20, 2023

    Alpha Thalassemia Major, Hemoglobinopathy; With Thalassemia, Hemoglobinopathies Trial in San Francisco (in utero hematopoietic

    Enrolling by invitation
    • Alpha Thalassemia Major
    • +8 more
    • in utero hematopoietic stem cell transplantation
    • San Francisco, California
      University of California
    Oct 28, 2022